The next generation of non-competitive pharmacological chaperones

Our mission is to improve the quality
of life of those suffering from rare diseases, through the discovery and development of innovative therapeutic agents.

New hope for people suffering from inborn errors of metabolism

Our mission is to improve the quality
of life of those suffering from rare diseases, through the discovery and development of innovative therapeutic agents.

A cure for life-threatening rare diseases

Our mission is to improve the quality
of life of those suffering from rare diseases, through the discovery and development of innovative therapeutic agents.

Towards a pharmacological therapy for Adrenoluekodystrophy

Our mission is to improve the quality
of life of those suffering from rare diseases, through the discovery and development of innovative therapeutic agents.

  • SEE-Tx ™ destacat_1

    An innovative technological platform to identify a new class of pharmacological chaperones non-competitive with the natural substrate.

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  • GM1 gangliosidosis destacat_2

    An extremely severe neurometabolic disease, particularly for children, and without treatment on the market.

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  • Adrenoleukodystrophy destacat_4

    A rare inherited peroxisomal neurodegenerative disorder, chronically debilitating and life threatening.

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The Company

A patient oriented company driven by passion

Pipeline

Focused on neurometabolic diseases without cure

Pharmacological chaperones

Rescuing the biological activity of mutant proteins

Press Releases

News